Antisense Oligonucleotide Suppression of C9orf72
Episode 16 min 40s

Antisense Oligonucleotide Suppression of C9orf72

From Neurology® Podcast American Academy of Neurology

Dr. Jeff Ratliff discusses the suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide with Drs. Jonathan Watts and Robert Brown.

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